Allogeneic hematopoietic SCT as treatment option for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE) : a consensus conference proposal for a standardized approach
JournalArticle (Originalarbeit in einer wissenschaftlichen Zeitschrift)
 
ID 1196413
Author(s) Halter, J; Schüpbach, W M M; Casali, C; Elhasid, R; Fay, K; Hammans, S; Illa, I; Kappeler, L; Krähenbühl, S; Lehmann, T; Mandel, H; Marti, R; Mattle, H; Orchard, K; Savage, D; Sue, C M; Valcarcel, D; Gratwohl, A; Hirano, M
Author(s) at UniBasel Krähenbühl, Stephan
Year 2011
Title Allogeneic hematopoietic SCT as treatment option for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE) : a consensus conference proposal for a standardized approach
Journal Bone marrow transplantation
Volume 46
Number 3
Pages / Article-Number 330-7
Keywords allogeneic hematopoietic SCT, mitochondrial neurogastrointestinal encephalomyopathy, MNGIE, consensus, recommendation
Abstract Allogeneic hematopoietic SCT (HSCT) has been proposed as a treatment for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE). HSCT has been performed in nine patients using different protocols with varying success. Based on this preliminary experience, participants of the first consensus conference propose a common approach to allogeneic HSCT in MNGIE. Standardization of the transplant protocol and the clinical and biochemical assessments will allow evaluation of the safety and efficacy of HSCT as well as optimization of therapy for patients with MNGIE.
Publisher Nature Publishing Group
ISSN/ISBN 0268-3369
edoc-URL http://edoc.unibas.ch/dok/A6006584
Full Text on edoc No
Digital Object Identifier DOI 10.1038/bmt.2010.100
PubMed ID http://www.ncbi.nlm.nih.gov/pubmed/20436523
ISI-Number WOS:000288164000002
Document type (ISI) Consensus Development Conference, Journal Article
 
   

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